Nxera Pharma Licenses Japan and Select Asia-Pacific Rights to Vamorolone for Duchenne Muscular Dystrophy from Santhera Pharmaceuticals

Vamorolone is approved and marketed as AGAMREE® for the treatment of Duchenne Muscular Dystrophy (DMD) in the US, European Union, UK and ChinaNew ...
Houston Public Media

Gene therapy for muscular dystrophy stirs hopes and controversy

Susan and Chris Finazzo have enrolled their sons Dylan and Chase in a study of gene therapy for Duchenne muscular dystrophy. The experimental treatment is still being studied but researchers hope it ...
LAist

Muscular dystrophy patients get first gene therapy

In an eagerly anticipated decision, the Food and Drug Administration Thursday approved the first gene therapy for muscular dystrophy. "Today's approval addresses an urgent unmet medical need and is an ...
KETV Omaha

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young kids

Muscular dystrophy is *** debilitating condition affecting one's ability to move around the world. There is currently no cure for the disease which is why some are now turning to technology to live ** ...
The American Journal of Managed Care

Developments in Muscular Dystrophy Gene Therapy

Emma Ciafaloni, MD, FAAN, dives into the latest developments in gene therapy for muscular dystrophies, focusing on Duchenne muscular dystrophy, and discusses challenges, genetic causes, and the ...
WMUR

FDA expands approval of first gene therapy for rare form of muscular dystrophy

The U.S. Food and Drug Administration has given the green light for the first gene therapy that treats a rare form of muscular dystrophy to be used in most people who have the disease and a certain ...
KPBS

Gene therapy for muscular dystrophy stirs hopes and controversy

When Chase Finazzo was just a few years old, his parents noticed Chase was pretty clumsy. But they didn't think it was anything serious. "He would fall a lot. Not like a lot a lot. But he had trouble ...
WLWT

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young kids

The first gene therapy for a deadly form of muscular dystrophy received preliminary U.S. approval on Thursday despite concerns from some government scientists about the treatment's ability to help ...
LAist

Gene therapy for muscular dystrophy stirs hopes and controversy

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